A New Advent in Hemophilia: Healthcare Economics Associated With Emerging Gene Therapies
uniQure.
Faculty Presenter
Surabhi Palkimas, PharmD
Clinical Pharmacist, Benign Hematology Clinic
University of Colorado Hospital
Blood Disorder Center
Aurora, Colorado
Clinical Assistant Professor
Skaggs School of Pharmacy and Pharmaceutical Sciences
Aurora, Colorado
Program Description
Hemophilia treatment is lifelong and requires repeated infusions of either plasma-derived or recombinant factor VIII or IX into the bloodstream 2 or 3 times weekly, or in response to bleeding. However, gene therapy is emerging as a new paradigm in hemophilia treatment. It typically requires 1 infusion, and thus has the potential to significantly alleviate costs associated with on-demand treatment for hospitalizations or for patients receiving prophylactic treatment and reduce number of days missed from school or work. Managed care pharmacists should proactively review ongoing clinical trial data for gene therapies to be familiar with these treatment options as they enter the market to improve patient outcomes while considering healthcare resource utilization.
Target audience: Managed care and oncology pharmacists
Type of activity: Application
Release date: December 1, 2020
Expiration date: June 1, 2022
Time to complete activity: 1.0 hour
Fee: Free
Educational Objectives
At the completion of this activity, participants will be able to:
• Examine the clinical and economic impact of acute and long-term bleeding events for patients with hemophilia.
• Demonstrate current standards of care for hemophilia and the potential role of gene therapies in treatment.
• Illustrate the burden of complications associated with hemophilia, including hospitalizations, factor replacement, and emergency department utilization data.

Pharmacy Times Continuing Education™ is accredited by the Accreditation Council for Pharmacy Education (ACPE) as a provider of continuing pharmacy education. This activity is approved for 1.0 contact hour (0.10 CEU) under the ACPE universal activity number 0290-0000-20-381-H01-P. The activity is available for CE credit through June 1, 2022.
Instructions for Completing the Activity and Receiving CPE Credit
To receive CPE credit, participants must complete the pretest, view the webinar in its entirety, complete the posttest, and complete the online activity evaluation. After successful completion of the online activity evaluation, you can submit your credit to CPE Monitor. You may view your credit within 48 hours at www.mycpemonitor.net. All participants must request credit before the activity expiration date. CE credit will not be issued after this date.
Disclosures
Surabhi Palkimas, PharmD, has no relevant financial relationships with commercial interests to disclose.
Pharmacy Times Continuing Education™ Planning Staff – Jim Palatine, RPh, MBA; Maryjo Dixon, RPh; Meg Taylor, PharmD, CPP; Kelly McCormick; Susan Pordon; and Brianna Winters have no financial relationships with commercial interests to disclose.
An anonymous peer reviewer is used as part of content validation and conflict resolution. The peer reviewer has no relevant financial relationships with commercial interests to disclose.
Educational Disclaimer
CPE activities are offered solely for educational purposes and do not constitute any form of professional advice or referral. Discussions concerning drugs, dosages, and procedures may reflect the clinical experience of the author(s) or they may be derived from the professional literature or other sources and may suggest uses that are investigational in nature and not approved labeling or indications. Participants are encouraged to refer to primary references or full prescribing information resources.
For questions about this internet CPE activity, please contact:
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